| Aldurazyme 100 U/ml concentrate for solution for infusion SPC (A16AB05 laronidase) |
Prescription only (POM) |
| Ammonaps 500 mg tablets SPC (A16AX03 sodium phenylbutyrate) |
Prescription only (POM) |
| Brineura SPC (A16AB Enzymes for alimentary tract and metabolism) |
Prescription only (POM) |
| Brineura 150 mg solution for infusion SPC (A16AB17 cerliponase alfa) |
Prescription only (POM) |
| Carbaglu SPC (A16AA05 carglumic acid) |
Prescription only (POM) |
| Carbaglu 200 mg dispersible tablets SPC (A16AA05 carglumic acid) |
Prescription only (POM) |
| Carglumic Acid Waymade 200 mg dispersible tablets SPC (A16AA05 carglumic acid) |
Prescription only (POM) |
| Carnitor 1 g chewable tablets / Levocarnitine 1 g chewable tablets not available (A16AA01 levocarnitine) |
– |
| Carnitor 1 g oral solution no longer supplied (A16AA01 levocarnitine) |
– |
| Carnitor 1 g solution for injection SPC no longer supplied (A16AA01 levocarnitine) |
– |
| Cerdelga 21 mg hard capsules SPC (A16AX10 eliglustat) |
Prescription only (POM) |
| Cerdelga 84 mg hard capsules SPC (A16AX10 eliglustat) |
Prescription only (POM) |
| Cerezyme 400 units powder for concentrate for solution for infusion SPC (A16AB02 imiglucerase) |
Prescription only (POM) |
| Cufence SPC (A16A Other alimentary tract and metabolism products) |
Prescription only (POM) |
| Cufence 100 mg hard capsules SPC (A16AX12 trientine) |
Prescription only (POM) |
| Cufence 200 mg hard capsules SPC (A16AX12 trientine) |
Prescription only (POM) |
| Cuprior SPC (A16AX Various alimentary tract and metabolism products) |
Prescription only (POM) |
| Cuprior 150 mg film-coated tablets SPC (A16AX12 trientine) |
Prescription only (POM) |
| Cystadane SPC (A16AA06 betaine) |
– |
| Cystadane 1 g oral powder SPC (A16AA06 betaine) |
Prescription only (POM) |
| Cystagon 150 mg hard capsules SPC (A16AA04 mercaptamine) |
Prescription only (POM) |
| Cystagon 50 mg hard capsules SPC (A16AA04 mercaptamine) |
Prescription only (POM) |
| Elaprase 2 mg / ml concentrate for solution for infusion SPC (A16AB09 idursulfase) |
Prescription only (POM) |
| Fabrazyme 35 mg powder for concentrate for solution for infusion SPC (A16AB04 agalsidase beta) |
Prescription only (POM) |
| Fabrazyme 5 mg powder for concentrate for solution for infusion SPC (A16AB04 agalsidase beta) |
Prescription only (POM) |
| Galafold 123 mg hard capsules (A16AX Various alimentary tract and metabolism products) |
Prescription only (POM) |
| Givlaari 189 mg / ml solution for injection SPC (A16AX16 givosiran) |
Prescription only (POM) |
| Kanuma 2 mg / ml concentrate for solution for infusion SPC |
Prescription only (POM) |
| Kuvan 100 mg powder for oral solution SPC no longer supplied (A16AX07 sapropterin) |
– |
| Kuvan 100 mg soluble tablets SPC no longer supplied (A16AX07 sapropterin) |
– |
| Kuvan 500 mg powder for oral solution SPC no longer supplied (A16AX07 sapropterin) |
– |
| Lamzede 10 mg powder for solution for infusion SPC (A16AB15 velmanase alfa) |
Prescription only (POM) |
| Levocarnitine 1 g chewable tablets, Carnitor 1 g chewable tablets not available (A16AA01 levocarnitine) |
– |
| Levocarnitine 1 g oral solution, Carnitor 1 g oral solution (A16AA01 levocarnitine) |
Prescription only (POM) |
| Levocarnitine 1 g solution for injection SPC (A16AA01 levocarnitine) |
Prescription only (POM) |
| Levocarnitine paediatric 30% oral solution, Carnitor paediatric 30% oral solution (A16AA01 levocarnitine) |
Prescription only (POM) |
| Mepsevii SPC (A16AB18 vestronidase alfa) |
Prescription only (POM) |
| Mepsevii 2 mg / ml concentrate for solution for infusion SPC (A16AB18 vestronidase alfa) |
Prescription only (POM) |
| Miglustat 100 mg hard capsules SPC (A16AX06 miglustat) |
Prescription only (POM) |
| Miglustat Dipharma SPC (A16AX06 miglustat) |
– |
| Miglustat Dipharma 100 mg hard capsules SPC (A16AX06 miglustat) |
Prescription only (POM) |
| Miglustat Gen.Orph 100 mg hard capsules SPC (A16AX06 miglustat) |
Prescription only (POM) |
| Myalepta 11.3 mg powder for solution for injection SPC (A16AA Amino acids and derivatives) |
Prescription only (POM) |
| Myalepta 3 mg powder for solution for injection. (A16AA07 metreleptin) |
Prescription only (POM) |
| Myalepta 5.8 mg powder for solution for injection SPC (A16AA07 metreleptin) |
Prescription only (POM) |
| Myozyme SPC (A16AB07 alglucosidase alfa) |
Prescription only (POM) |
| Myozyme 50 mg powder for concentrate for solution for infusion SPC (A16AB07 alglucosidase alfa) |
Prescription only (POM) |
| Naglazyme 1 mg/ml concentrate for solution for infusion SPC (A16AB Enzymes for alimentary tract and metabolism) |
Prescription only (POM) |
| Nitisinone 10 mg hard capsules (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone 2 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone 5 mg hard capsules (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone Dipharma 10 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone Dipharma 2 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone Dipharma 20 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone Dipharma 5 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone MDK (previously Nitisinone MendeliKABS) SPC (A16AX04 nitisinone) |
– |
| Nitisinone MDK 10 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nitisinone MDK 2 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Nityr 10 mg tablets SPC (A16AX04 nitisinone) |
– |
| Opfolda 65 mg hard capsules SPC (A16AX06 miglustat) |
Prescription only (POM) |
| Orfadin 10 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Orfadin 2 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Orfadin 20 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Orfadin 4 mg / ml oral suspension SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Orfadin 5 mg hard capsules SPC (A16AX04 nitisinone) |
Prescription only (POM) |
| Oxlumo SPC (A16AX18 lumasiran) |
Prescription only (POM) |
| Oxlumo 94.5 mg / 0.5 ml solution for injection SPC (A16AX18 lumasiran) |
Prescription only (POM) |
| Palynziq SPC (A16AB19 pegvaliase) |
– |
| Pheburane 350 mg/ml oral solution (A16AX03 sodium phenylbutyrate) |
Prescription only (POM) |
| Procysbi 25 mg gastro-resistant hard capsules SPC (A16AA04 mercaptamine) |
Prescription only (POM) |
| Procysbi 300 mg gastro-resistant granules SPC (A16AA04 mercaptamine) |
Prescription only (POM) |
| Procysbi 75 mg gastro-resistant granules SPC (A16AA04 mercaptamine) |
Prescription only (POM) |
| Procysbi 75 mg gastro-resistant hard capsules SPC (A16AA04 mercaptamine) |
Prescription only (POM) |
| Ravicti 1.1 g/ml oral liquid SPC (A16AX09 glycerol phenylbutyrate) |
Prescription only (POM) |
| Replagal 1 mg / ml concentrate for solution for infusion SPC no longer supplied (A16AB03 agalsidase alfa) |
– |
| Revestive 5 mg powder and solvent for solution for injection SPC (A16AX08 teduglutide) |
Prescription only (POM) |
| Sapropterin Dihydrochloride 100 mg powder for oral solution SPC (A16AX07 sapropterin) |
– |
| Sapropterin Dihydrochloride 100 mg soluble tablets SPC (A16AX07 sapropterin) |
Prescription only (POM) |
| Sapropterin Dihydrochloride 500 mg powder for oral solution SPC (A16AX07 sapropterin) |
– |
| Strensiq 100 mg / ml solution for injection (A16AB13 asfotase alfa) |
Prescription only (POM) |
| Strensiq 40 mg / ml solution for injection SPC (A16AB Enzymes for alimentary tract and metabolism) |
– |
| Teduglutide 5 mg powder and solvent for solution for injection SPC (A16AX08 teduglutide) |
Prescription only (POM) |
| Teduglutide Cipla 5 mg/vial powder and solvent for solution for injection (A16AX08 teduglutide) |
Prescription only (POM) |
| Trientine 200 mg hard capsules SPC (A16AX12 trientine) |
Prescription only (POM) |
| Trientine Dihydrochloride Tillomed 250 mg capsules SPC (A16AX12 trientine) |
Prescription only (POM) |
| Ucedane SPC (A16AA05 carglumic acid) |
Prescription only (POM) |
| Ucedane 200 mg dispersible tablets SPC (A16AA05 carglumic acid) |
Prescription only (POM) |
| Vimizim 1 mg / ml concentrate for solution for infusion SPC (A16AB12 elosulfase alfa) |
Prescription only (POM) |
| Vpriv SPC (A16AB10 velaglucerase alfa) |
Prescription only (POM) |
| Vpriv 400 units powder for solution for infusion SPC (A16AB10 velaglucerase alfa) |
Prescription only (POM) |
| Wilzin 25 mg hard capsules SPC (A16AX05 zinc acetate) |
Prescription only (POM) |
| Wilzin 50 mg hard capsules SPC (A16AX05 zinc acetate) |
Prescription only (POM) |
| Xermelo 250 mg film-coated tablets SPC (A16A Other alimentary tract and metabolism products) |
Prescription only (POM) |
| Yargesa 100 mg hard capsules SPC (A16AX06 miglustat) |
Prescription only (POM) |
| Zavesca 100 mg capsules SPC (A16AX06 miglustat) |
Prescription only (POM) |
